WILMINGTON, Del.--(BUSINESS WIRE)--Positive high-level results from the NEURO-TTRansform Phase III trial in patients with hereditary transthyretin-mediated amyloid polyneuropathy (ATTRv-PN) showed ...

Patients with hATTR amyloidosis who experience polyneuropathy progression post-OLT have a significant treatment need and the results of the Phase 3b study of patisiran demonstrated robust TTR ...

Please provide your email address to receive an email when new articles are posted on . Wainua has received regulatory approval for polyneuropathy of hereditary transthyretin-mediated amyloidosis.

Credit: Getty Images. Eplontersen is an investigational ligand-conjugated antisense medicine designed to reduce the production of TTR protein to treat both hereditary and nonhereditary forms of ATTR.

A possible new treatment option for transthyretin amyloidosis has shown promising results in an initial clinical trial. Transthyretin amyloidosis (ATTR amyloidosis) is a rare, progressive, and fatal ...

(RTTNews) - Ionis Pharmaceuticals Inc. (IONS) presented positive results from a planned 35-week interim analysis of the Phase 3 NEURO-TTRansform study of Ionis and AstraZeneca's eplontersen in ...

Please provide your email address to receive an email when new articles are posted on . While currently there is no cure for systemic amyloidosis, treatment options have recently expanded and have led ...

CARLSBAD, Calif., June 21, 2022 /PRNewswire/ -- Ionis Pharmaceuticals, Inc. (Nasdaq: IONS) today announced positive topline results from a 35-week interim analysis of the Phase 3 NEURO-TTRansform ...

—This cross-sectional study investigated a possible association between a high GI symptom burden in types 1 and 2 diabetes with the presence of various neuropathies. A high gastrointestinal (GI) ...

"Alterations in axonal membrane and channel function occur early in the disease course, prior to discernable large fibre involvement, and has the potential to be used as an early biomarker of ...

Hereditary transthyretin amyloidosis (hATTR) is a rare inherited disorder that gets worse over time. It often affects the nerves, heart, liver, and kidneys, but it can also affect other organs.

Monoclonal gammopathies represent a broad differential diagnosis and require a thorough evaluation for clinical significance. Smoldering multiple myeloma is a clinical entity that does not require ...