The agency's decision is based on results from a clinical trial in which the treatment improved hearing in 80 percent of the ...
Dr. Swee Lay Thein and Dr. Stuart Orkin won the $3 million Breakthrough Prize in Life Sciences for their work toward a ...
The treatment, the first of its kind, was approved by the Food and Drug Administration on Thursday. “Our baby was born deaf, ...
Married couple Jean Bennett and Albert Maguire developed Luxturna, which helped a patient see their child’s face for the first time ...
Forbes contributors publish independent expert analyses and insights. William A. Haseltine, Ph.D., covers genomics and regenerative medicine This voice experience is generated by AI. Learn more. This ...
A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain disorders known as SYNGAP1-related disorders, or SRDs. Researchers were able ...
A married couple of scientists has won the 2026 Breakthrough Prize in Life Sciences for creating the world's first gene ...
The idea behind intra-articular gene therapy for treating osteoarthritis (OA) is to deliver the gene-altering vector or cells directly to the precise site of the disease with a single injection — so ...
Forbes contributors publish independent expert analyses and insights. A patient in a late-stage gene editing trial for a rare heart condition died from fatal liver complications after receiving an ...
It began with a phone call from a lab technician: “They can see!” The ...
The US Food and Drug Administration on Thursday approved the first gene therapy for inherited hearing loss, a one-time ...