The development of gene editing tools, which enable the specific targeting and correction of mutations, hold the promise of allowing us to correct those mutations that cause genetic diseases. However, ...

Researchers have successfully develop single-atom editing technology that maximizes drug efficacy. In pioneering drug development, the new technology that enables the easy and rapid editing of key ...

A team of Chinese scientists has used gene therapy to correct a mutation that caused mice to exhibit autistic behaviors like hyperactivity, repetitive self-grooming, and abnormal social interactions.

At the heart of this technology is the Cas9 protein, often likened to molecular scissors, capable of cutting strands of DNA at specific locations dictated by a single guide RNA. With this mechanism, ...

Adenosine base editing restarted fetal hemoglobin expression in cells from patients with sickle cell disease. Gene therapy that alters hemoglobin genes may be an answer to curing sickle cell disease ...